Cures for Rett on the Horizon Webinar: Q&A Follow Up w/Monica скачать в хорошем качестве

Cures for Rett on the Horizon Webinar: Q&A Follow Up w/Monica

We've got some more answers from the Webinar Q&A, this time from Monica! More to come, and don't forget you can ask us questions any time you want via direct messages here, email, or phone! Helpful Links: Roadmap to Cures - https://reverserett.org/cures/ Rett Global Registry - https://reverserett.org/global-registry/ Jump to a specific question here: 0:00 Monica Intro 0:34 Genetic Medicines for Older Patients? 1:11 Gene Therapy for 2-year Old? 1:51 Update on Trials? 2:25 How are Patients Chosen for Trials? 3:01 How to get into Trials? 3:52. Will Cognitive Development Improve? 4:04 Which Roadmap Modality is Superior? 4:38 How Much will it Cost? 5:40 Will Insurance Cover Clinical Trials? 6:07 The Burden of Disease 7:09 Can Base Editing Fix Every Cell? 8:28 Genetic Medicines Global Availability 9:13 What Causes Mutations? 9:45 Confident that Solution is in MECP2? 10:08 Is it Foolish to Wait for Gene Therapy?