Inside the AAV9-NF2 Gene Therapy Approach скачать в хорошем качестве

Inside the AAV9-NF2 Gene Therapy Approach

NF2 BioSolutions Webinar: AAV9-NF2 Gene Therapy – A New Approach to Treat NF2 📅 Recorded: May 29, 2025 In this NF2 Awareness Month webinar, NF2 BioSolutions hosted an expert panel to discuss a promising new AAV9-based gene therapy approach to treating NF2. Led by Dr. Kathrin Meyer (Nationwide Children’s Hospital), Dr. Gary Brenner (Massachusetts General Hospital), and Krizelle Alcantara, the discussion highlights the ongoing development of a gene addition therapy designed to insert a functional copy of the NF2 gene into cells—aiming to halt or prevent tumor growth. Topics covered include: The science behind AAV9 vector delivery How gene addition differs from editing Project development progress Challenges and next steps toward clinical trials What this means for the NF2 community 🎤 Moderated by Mary Sell, NF2 parent. 📌 Learn more at: https://nf2biosolutions.org/ #NF2 #GeneTherapy #AAV9 #NF2Awareness #NF2Research #Neurofibromatosis #NF2Webinar #RareDisease #Neurogenetics #Geneaddition