Cell & Gene Exchange, May 2017: Généthon скачать в хорошем качестве

Cell & Gene Exchange, May 2017: Généthon

Généthon, created by the AFM-Telethon, is dedicated to making innovative gene therapy treatments available to patients affected with rare genetic diseases. Having played a pioneering role in deciphering the human genome, Généthon is today, with more than 120 scientists, physicians, engineers and regulatory affairs specialists, one of the leading organizations for the development of gene therapy treatments. Généthon has also built one of the largest sites worldwide for GMP-production of gene therapy products, that was incorporated in 2016 into YposKesi, a company created with the investment of AFM-Telethon and BPI-France, in order to address the challenges of industrializing cell and gene therapy methods. Généthon was awarded the prestigious Prix Galien for Pharmaceutical Research (France) in 2012. In 2015, Genethon was one of 16 winners of the World Innovation Competition 2030 for its project on the development of an industrial process for production of gene therapy vectors. The pipeline of Généthon includes products currently in international clinical trials and at preclinical stages, for immune deficiencies, muscular dystrophies, blood and liver diseases. These products are developed either with Généthon as sponsor, or in partnership with private companies and academic institutions. www.genethon.com Speaker: Revah Frédéric – CEO