🔵 [NEO CONFERENCE] - Where Will Gene Therapy Be in 10 Years? (Dr. Barry Birne) скачать в хорошем качестве

🔵 [NEO CONFERENCE] - Where Will Gene Therapy Be in 10 Years? (Dr. Barry Birne)

Live from the NEO conference in Las Vegas, Ben and Daphna sit down with Dr. Barry Birne from the University of Florida for a wide-ranging conversation on the present and future of gene therapy. From the radical transformation of SMA care since 2019 to the logistical and ethical complexity of treating a preterm baby identified through newborn screening, Dr. Birne makes the case that neonatologists need to understand this space now. The conversation covers gene editing, lipid nanoparticles, CAR-T cells, and the economic realities families face navigating multi-million dollar treatments. A thought-provoking reminder that families cannot afford to go a day without hope.