Gene Therapy Basics for Hemophilia: What You Need to Know скачать в хорошем качестве

Gene Therapy Basics for Hemophilia: What You Need to Know

Recently there has been an explosion of innovative research in the treatment of Hemophilia utilizing gene therapy technology. This workshop will help you develop a basic understanding of the complexities of gene therapy including terminology, how gene therapy works, and identifying the potential, limitations, risks, and unknowns associated with gene therapy. We also provide a brief introduction to other novel therapies and an overview of what treatments are currently approved. Gaining a high-level understanding of gene therapy will enable community members to have robust conversations with their providers and ultimately make the best decision on treatment. The National Hemophilia Foundation is dedicated to finding better treatments and cures for inheritable bleeding disorders and to preventing the complications of these disorders through education, advocacy, and research.