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Visit https://www.asgct.org/education for more free resources on gene and cell therapy, including progress on a number of promising treatments already in development. Lots of genetic diseases come down to a small change in a single gene, but how do you treat those diseases when the cells involved don’t have any DNA? Hosted by: Hank Green SciShow has a spinoff podcast! It's called SciShow Tangents. Check it out at https://www.scishowtangents.org ---------- Support SciShow by becoming a patron on Patreon: / scishow ---------- Dooblydoo thanks go to the following Patreon supporters: Alex Schuerch, Alex Hackman, Andrew Finley Brenan, Sam Lutfi, D.A. Noe, الخليفي سلطان, Piya Shedden, KatieMarie Magnone, Scott Satovsky Jr, Charles Southerland, Patrick D. Ashmore, charles george, Kevin Bealer, Chris Peters ---------- Looking for SciShow elsewhere on the internet? Facebook: / scishow Twitter: / scishow Tumblr: / scishow Instagram: / thescishow ---------- Sources: https://www.nature.com/articles/ng109... https://www.fda.gov/newsevents/newsro... https://www.ncbi.nlm.nih.gov/pmc/arti... https://www.ncbi.nlm.nih.gov/pubmed/1... https://ghr.nlm.nih.gov/condition/sic... https://www.sciencedirect.com/science... https://www.sciencedirect.com/science... https://www.nature.com/articles/549S28a https://www.nejm.org/doi/full/10.1056... https://clinicaltrials.gov/ct2/show/N... https://clinicaltrials.gov/ct2/show/N... http://science.sciencemag.org/content... https://www.nature.com/articles/s4137... https://www.ncbi.nlm.nih.gov/pmc/arti... https://www.nature.com/articles/natur... http://www.bloodjournal.org/content/e... https://www.the-scientist.com/news-op... Images: https://commons.wikimedia.org/wiki/Fi... https://commons.wikimedia.org/wiki/Fi... https://commons.wikimedia.org/wiki/Fi... https://commons.wikimedia.org/wiki/Fi... https://commons.wikimedia.org/wiki/Fi... https://www.istockphoto.com/vector/an... https://www.istockphoto.com/vector/3d... https://www.istockphoto.com/vector/he... https://www.istockphoto.com/photo/ins... https://www.istockphoto.com/vector/cu... https://www.istockphoto.com/photo/car... https://www.istockphoto.com/photo/bon... https://www.istockphoto.com/vector/hu... https://www.istockphoto.com/vector/st...