Kacper's AADC Gene Therapy Journey скачать в хорошем качестве

Kacper's AADC Gene Therapy Journey

Kacper was the first AADC child to receive Gene Therapy in Europe. We asked his mum, Ela, a few questions to give you an insight into the incredible difference this pioneering treatment has made to their lives in just 70 days! Ela has also provided us with a video diary of before and after Gene Therapy treatment. The changes may not be easily apparent to the eye of the viewer, but they hugely significant to Kacper and his family. It is still early days and the uptake of Dopamine into the brain can and will take some time. We are very excited to keep following Kacper’s amazing progress.... visit us at: www.aadcresearch.org